I-Machado-Joseph Disease Symptoms and Treatment

Isifo seMachado-Joseph (MJD), esaziwa nangokuthi i- spinocerebellar ataxia hlobo 3 (SCA3), sisifo se-ataxia esizuze njengefa. I-Ataxia inokuchaphazela ukulawulwa kwemisipha, okubangelwa ukungabikho kwemilinganiselo kunye nokulungelelaniswa. Ngokukodwa, i-MJD ibangela ukungaphumeleli kokuqhubeka kokulungelelanisa kwiingalo nasemilenzeni. Abantu abanemeko bavame ukuba nokuhamba okungafaniyo, okufana nokudakwa okudakwa.

Basenokuba nobunzima bokuthetha nokugwinya.

I-MJD idibaniswe nesiphene semfuyo kwi-ATXN3 yesigcine kwi- chromosome 14. Yiyo imeko ephezulu ye-autosomal, oku kuthetha ukuba umzali omnye kuphela kufuneka abe ne-gene yokuchaphazeleka komntwana. Ukuba unesimo, umntwana wakho unokufumana ithuba lokufumana ilifa le-50%. Le meko ibonakala kakhulu kubantu basePutukezi okanye kwi-Azorean desccent. Kwisiqithi sase-Flores kwi-Azores, abantu abayi-1 kwabangu-140 bachaphazelekayo. Nangona kunjalo, i-MJD iyakwenzeka nakweyiphi na indawo.

Iimpawu

Kukho iintlobo ezahlukeneyo zeMJD. Yiyiphi uhlobo oxhomekeke kuyo xa iimpawu ziqala kunye nobukhulu bezo zimpawu. Nantsi ukujonga kwiimpawu eziqhelekileyo kunye neempawu zontlobo ezintathu:

Uhlobo Ubudala bokuqala Ubunzima beMpawu kunye noPhuculo Iimpawu
Uhlobo I (MKD-I) Phakathi kweminyaka eyi-10-30 ubudala Ubunzima beSimptom buqhubeka ngokukhawuleza
  • Izidumbu ezincinci (i- dystonia )
  • Ubunzima (ubunzima)
Uhlobo II (MJD-II) Phakathi kweminyaka engama-20 ukuya kuma-50 ubudala Iimpawu zibuhlungu ngokukhawuleza ngokuhamba kwesikhathi
  • Ukuqhubela phambili kwemisipha engalawulwayo (ukungabi nesikhala)
  • Ubunzima bokuhamba ngenxa ye-spasms spasms (spastic gait)
  • Iingcamango ezingekhoyo
Uhlobo III (MJD-III) Phakathi kweminyaka engama-40-70 ubudala Iimpawu ziba nzima ngakumbi ngexesha
  • Ukuguqulwa kwamathambo
  • Ubungqingili, ukubetha, iingqumbo, nentlungu ezandleni, ezinyaweni, iingalo kunye nemilenze (i-neuropathy)
  • Ukulahlekelwa kwezicubu zesisu (i-atrophy)

Abantu abaninzi abane-MJD banemibono yombono njengemibono emibini (diplopia) kunye nokukwazi ukulawula ukunyakaza kwamehlo, kunye nokuthuthumela kwezandla zabo kunye neengxaki ngokulinganisela nokulungelelanisa. Abanye banokuhlakulela ubuso okanye iingxaki zokucima.

I-MJD ichongwa njani

I-MJD ifunyaniswa ngokusekelwe kwiimpawu ozifumanayo.

Ekubeni i- disorder ilifa , kubalulekile ukujonga kwimbali yakho yentsapho. Ukuba izalamane zinempawu ze-MJD, zibuze xa iimpawu zabo zaqala kwaye zikhawuleza ziphuhlise njani. Ukuxilongwa ngokuqinisekileyo kunokuvela kuphela kuvavanyo lwemizimba, oluza kubheka iziphene kwi-chromosome yakho yesi-14. Kwabo baphila ngokuqala kwe-MJD, ukulinda ubomi kunokuba mfutshane nje nge-30s. Abo bane-MJD emninzi okanye uhlobo olusemva kwexesha elide, ngokuqhelekileyo banomdla wokuhlala ngokuqhelekileyo.

Unyango

Okwangoku, akukho nonyango yeMachado-Joseph. Sinawo indlela yokumisa iimpawu zayo ekuqhubekeni. Kukho, nangona kunjalo, amayeza anokunceda ukukhupha iimpawu. I-Baclofen (i-Lioresal) okanye i-toxin ye-botulin (iBotox) inokukunceda ukunciphisa ama-muscle spasms kunye ne-dystonia. Ukwelashwa kwe-Levodopa, unyango olwenzelwe abantu abane-Parkinson isifo, kunokukunceda ukunciphisa ubunzima nokuphuculwa. Ukwelapha umzimba kunye nezixhobo zokuncedisa kunokunceda abantu abaneentshukumo nemisebenzi yemihla ngemihla. Ukubonakalisa iimpawu ezibonakalayo, iziglasi zengqungquthela zinokunceda ukunciphisa umbono obonakele okanye obini.

Imithombo:

"Machado-Joseph Fact Sheet." Ngxaki. Ngomhla wama-16 kuMatshi 2014. Isiko seSizwe seNational Psychology and Stroke.

"Machado-Joseph Disease." Index of the Rare Diseases. I-National Organisation for Distress Disorders. 15 Feb 2007.