I-Schwartz-Jampel Syndrome: I-Rare, Inherited Disorder

Iimpawu, iiMbangela kunye noPiliso lweSystem Syndrome

I-Schwartz-Jampel syndrome (i-SJS) yintlupheko engaqhelekanga, ezuze ilifa elibangela ukungaqhelekanga kwezihlunu zamathambo.

Ezinye zezinto ezingaqhelekanga ezibangelwa yi-disorder zibandakanya oku kulandelayo:

I-SJS ithathwa njenge-autosomal condition condition, ebonisa ukuba umntu ufuna ukuzuza iimbumba ezimbini eziphosakeleyo, omnye kumzali ngamnye, ukwenzela ukuphuhlisa i-syndrome.

Iintlobo ze-Schwartz-Jampel Syndrome

Kukho iincinci eziningana zeSwitch-Jampel syndrome. Uhlobo I, olucatshangelwa uhlobo oluthile, lunamacandelo amabini anesigxina afunyenwe kwi-gene defective kwi-chromosome 1:

I-Schwartz-Jampel syndrome Uhlobo II lubonakala ngokukhawuleza ekuzalweni. Unempawu ezahlukileyo kunokuba i-IA okanye i-IB kwaye ayihambelananga nayo nayiphina impazamo yesini kwi-chromosome enye.

Ngako-ke, ezininzi iingcali zikholelwa ukuba uhlobo lwe-II luyisifo esifanayo neStuve-Wiedermann syndrome-ingxaki engaqhelekanga kunye neyobuhlungu obunomdla obuninzi kakhulu ekufeni kwiinyanga ezimbalwa zokuqala zokuphila, ngenxa yeengxaki zokuphefumla.

Ngaloo ndlela, Uhlobo I luza kugxininiswa kweli nqaku.

Iimpawu zeSJS

Uphawu oluphambili lweSwitwzz-Jampel syndrome luyimisipha yobunzima. Olu lukhuni lufana nolwe-Stiff-person syndrome okanye i- Isaacs syndrome , kodwa ukuqina kwesifo se-Schwartz-Jampel akukhululwa yimithi okanye ukulala. Izimpawu ezongezelelweyo ze-SJS zingaquka:

Kubalulekile ukuqonda ukuba zonke iimeko ze-SJS zihlukile kwaye zihluka kwibala kunye nobuqhamo beempawu ezihambelanayo, kuxhomekeke kuhlobo lwesifo.

Indlela UmGaqo-nkcukacha Oyafunyanwa Ngayo

I-SJS idla ngokubonakala ngexesha leminyaka yokuqala yobomi, ngokuqhelekileyo ekuzalweni. Abazali banokubona isisu esinzima sentsana ngexesha lokutshintsha i-diaper, umzekelo. Olu bunzima kunye neembonakalo zobuso eziqhelekileyo kwi-syndrome zihlala zikhomba ukuxilongwa .

Izifundo ezongezelelweyo ezifana ne-x-ray, i-biopsy, i-muscle biopsy, iimvavanyo zegazi ze-enzyme zegazi, kunye neemvavanyo ze-muscle kunye ne-nerve conduction emntwaneni ziya kwenziwa ukwenzela ukuqinisekisa ukungalingani okuhambisana ne-SJS. Ukuvavanya kwe-Genetic yesini esingenasiphelo kwi-chromosome 1 (i-gene HSPG2) nayo ingakuqinisekisa ukuxilongwa.

Kwezinye iimeko ezinqabileyo, ngaphambi kokubeleka (ukuzalwa ngaphambi kokuzalwa) ukuxilongwa kwe-SJS kunokunokwenzeka ngokusebenzisa ukusebenzisa i-ultrasound ukubona ukuba umntwana lowo unempawu ezikhomba i-SJS okanye ezinye izinto eziphuculweyo.

Izizathu zeSwitwz-Jampel Syndrome

Ekubeni i-SJS izuze ifa ngokweendlela zokuzimela, xa umntu ezalwa ene-syndrome bobabini abazali bakhe bayithwala i-gene defective. Umntwana ngamnye ozayo aba bazali abaya kuba nako 1 kwithuba eli-4 lokuzalwa kunye nesifo. Ngokuqhelekileyo, i-SJS ikholelwa ukuba ilifa kwi-autosomal pattern pattern. Kule meko, enye i-gene ekhubazekayo kufuneka izuzwe ilifa ukuba libonakalise.

Ngokubanzi, i-SJS yintlupheko engaqhelekanga enama-129 aqoshiwe amacala, ngokweengxelo kwi- Advanced Biomedical Research . I-SJS ayifutshane nokuphila, kwaye amadoda kunye nabasetyhini bachaphazeleka ngokufanayo ngesifo.

Uhlobo lwe-SJS II (olubizwa ngokuba yi-Stuve-Wiedermann syndrome) lubonakala luxhaphake kubantu abathile be-United Arab Emirates.

Unyango lweSwitch-Jampel Syndrome

Akukho nonyango yeSwitzerland-Jampel syndrome, ngoko unyango lujolise ekunciphiseni iimpawu zesifo. Amachiza anceda kwezinye izifo zengxubevange, ezinjengeyeza elixhatshazwayo i-Tegretol (carbamazepine) kunye neyeza-anti-arrhythic mexiletine inokuba luncedo.

Nangona kunjalo, ukuqina kobuhlungu emzimbeni eSwitzz-Jampel syndrome kungadluka ngokukhawuleza ngexesha elide, ngoko ukusebenzisa iindlela ngaphandle kokuba amayeza angakhetha. Ezi ziquka ukuxilwa kwe-muscle, ukufudumala, ukulula, nokufudumala ngaphambi kokuzivocavoca.

Ukuhlinzwa ukunyanga okanye ukulungisa ukungaqhelekanga kwemisipha, ezifana nezivumelwano ezidibeneyo, i-kyphoscoliosis (apho umjikelezo womlenze ungabonakaliyo) kunye ne-hip dysplasia inokukhetha ukuba iziguli ezithile ze-SJS. Kweminye, utyando oludibeneyo kunye nolwaphulo olunokwenyama lunokunceda ukuphucula ikhono lokuhamba kunye nokwenza olunye uhambo ngokuzimela.

Iingxaki ezibonakalayo neyamehlo, ukuhlinzwa, iilazi zokulungisa, ii-lens, i-Botox (ukwenzela i-eyelid), okanye ezinye iindlela zokuncedisa zinganceda ukuphucula umbono.

Imithombo:

J. J. (2014). iMedicine: I-Schwartz-Jampel syndrome.

Basiri K, Fatehi F, Katirji B. I-Schwartz-Jampel syndrome: Ingxelo yenkcazo kunye nokuhlaziywa kweencwadi. Adv Biomed Res. 2015; 4: 163.

Begam MA. I-Alsafi W, i-Bekdache GN, i-Chedid F, i-Al-Gazali L, iMirghani iHM. Isifundo-Wiedemann syndrome: i-dysplasia ye-skeletal ebonakaliswe ngamathambo amaninzi. Gynecol ye-Ultrasound Obstet. 2011 Nov; 38 (5): 553-8.

I-National Organisation for Distress Disorders. (2016). Schwartz-Jampel Syndrome.